Project Details
Description
I currently serve as a scientific advisor and collaborator with the Department of Systems Biology at MGH. In this role, I have actively contributed to the development and application of diagnostic technologies aimed at improving patient outcomes in the context of gene therapy.
Key findings
Development and application of diagnostic technologies aimed at improving patient outcomes in the context of gene therapy. This method provides biomarkers promising to improve management of sickle cell patients and to optimize the development and prioritization of candidate cures, and it’s currently used to validate the efficacy of BCL11A as therapeutic target in Sickle Cell Disease, Clinical Trials Identifier: NCT03282656 (Sponsor: David Williams – Boston Children’s Hospital).
Short title | Scientific advisor at MGH/HMS |
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Status | Active |
Effective start/end date | 1/09/16 → … |
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